Gene Therapy News — ScienceDaily
Liver Cancer Study Encourages Caution With Certain Gene Therapies
Dec. 7, 2022 Research has found that misfolded proteins in liver cells contribute to the development of liver cancer, shedding new light on the mysterious origins of one of the world’s deadliest diseases. …
Establishment of a Pancreatic Cancer Animal Model Using the Pancreas-Targeted Hydrodynamic Gene Delivery Method
Apr. 22, 2022 Pancreatic cancer has a significantly poor prognosis; therefore, the development of effective treatments is an unmet clinical need. The major drawback in this field was the lack of useful model …
Novel Nuclear microRNA Is Being Developed for the Treatment of Cardiovascular Disease
Apr. 1, 2022 A novel angiogenic microRNA drug can be a new option for the treatment of ischemic cardiovascular disease, according to a new study. In the study, the researchers describe a novel nuclear acting …
An Approach to Treating a Severe Congenital Myopathy
Mar. 29, 2022 The diagnosis is rare, but devastating — children with congenital muscle disorders often never learn to walk. Until now, there was no chance of recovery, but researchers are now presenting a …
How a Two-Faced Molecule Can Silence Problematic Genes
Feb. 28, 2022 Researchers have developed a technology, heteroduplex oligonucleotide (HDO), that silences certain genes whose high expression levels fuel disease. Adding a specific molecular tag allowed them to …
A Possible Cure for Sickle Cell?
Feb. 16, 2022 Sickle cell anemia is an inherited blood disorder where red blood cells become sickle/crescent shaped. It causes frequent infections, swelling in the hands and legs, pain, severe tiredness and …
My Heart Will Go On: Patient-Derived Heart Cells Mimic Disease in Vitro
Jan. 24, 2022 Researchers have found that induced pluripotent stem cell–derived cardiomyocytes from a patient with arrhythmogenic cardiomyopathy recapitulate the reduced contractility and impaired desmosome …
Calcium: Important Not Just for Your Bones but Also for Your Heart
Jan. 19, 2022 Researchers found a previously unknown gene mutation that can cause an incurable heart condition called dilated cardiomyopathy. This gene, BAC5, is important for the movement of calcium ions in the …
Epilepsy Research Boosts Case for New Gene Therapy for Dravet Syndrome
Jan. 19, 2022 New research suggests how a newly developed gene therapy can treat Dravet syndrome, a severe form of epilepsy, and potentially prolong survival for people with the …
New Gene Therapy Approach Offers a Potential Long-Term Treatment for Limb-Girdle Muscular Dystrophy 2B
Jan. 4, 2022 Medical experts have developed a new pre-clinical gene therapy for a rare disorder, known as limb-girdle muscular dystrophy (LGMD) 2B, that addresses the primary cellular deficit associated with this …
Experimental Gene Therapy Reverses Sickle Cell Disease for Years
Dec. 13, 2021 An experimental gene therapy for sickle cell disease restored blood cells to their normal shape and eliminated severe pain crises for years after treatment, a multicenter study has …
Gene Network Changes Associated With Cancer Onset and Progression Identify New Treatment Targets
Dec. 13, 2021 Researchers have identified novel changes in gene network interactions associated with cancer that may lead to new treatment targets for chemotherapy. Their work shows that more than 90 percent of …
CRISPR/Cas9 Gene Editing Boosts Effectiveness of Ultrasound Cancer Therapy
Dec. 8, 2021 Sonodynamic therapy uses ultrasound in combination with drugs to release harmful reactive oxygen species (ROS) at the site of a tumor. However, the treatment isn’t very effective because cancer …
ALS Therapy Should Target Brain, Not Just Spine
Dec. 2, 2021 The brain is indeed a target for treating ALS (amyotrophic lateral sclerosis), scientists have discovered. This flips a long-standing belief the disease starts in the spinal motor neurons and any …
Novel Gene Therapy Platform Speeds Search for Ways to Cure Blindness
Oct. 19, 2021 A novel computational platform identifies top-performing viral vectors that could deliver gene therapies to the retina with maximum efficiency and …
Developing a Treatment for Vision Loss Through Transplant of Photoreceptor Precursors
Oct. 18, 2021 A recent study examining the therapeutic potential of photoreceptor precursors, derived from clinically compliant induced pluripotent stem cells (iPSC), has demonstrated the safety and therapeutic …
Researchers Identify Genetic Cause of Endometriosis and Reveal Potential Drug Target
Aug. 25, 2021 New research offers insight into how to treat endometriosis. The researchers performed genetic analyses of humans and rhesus macaques to identify a specific gene, NPSR1, that increases risk of …
Teaching an Old Dog New Tricks: An Existing Drug Opens New Possibilities for Treating Childhood Leukemia
Aug. 24, 2021 A new study has shown that the tumor-inhibiting gene TET2 is silenced in a large fraction of cases of acute lymphoblastic leukemia (ALL) in children. The scientists show that the gene can be …
Researchers Develop ‘Dimmer Switch’ to Help Control Gene Therapy
July 28, 2021 In a major advancement in the field of gene therapy for rare and devastating diseases, researchers have developed a “dimmer switch” system that can control levels of proteins expressed from …
Innovative Gene Therapy ‘Reprograms’ Cells to Reverse Neurological Deficiencies
July 12, 2021 A novel method of gene therapy is helping children born with a rare genetic disorder called AADC deficiency that causes severe physical and developmental disabilities. The study offers new hope to …
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Source link Gene Therapy News, as reported by ScienceDaily, has become a beacon of hope for many, heralding great changes for the medical profession and for those who wait patiently for treatments for hereditary diseases.
Gene Therapy is a revolutionary new way of treating certain inherited and otherwise untreatable diseases. It is including replacing or correcting faulty genes which causes diseases. The treatment increases patient’s natural defence mechanisms by introducing corrective genes into the body.
ScienceDaily reported the news with awe, highlighting the new advancements in research that are taking the medical world by storm. It highlighted the various breakthroughs in different forms of gene therapy such as gene editing, vector-based therapy, and genome engineering.
Gene therapy is currently being used to treat diseases such as cancer, blood disorders, cystic fibrosis and HIV. Not only is this therapy breaking new ground in the field of medicine, it is also offering new hope to those suffering from incurable illnesses.
The news reported by ScienceDaily has been very encouraging and exciting, as it offers hope to many families who have previously been unable to acquire treatments for their loved ones.
Gene therapy is a powerful tool for treating diseases in ways that were previously unheard of. As ScienceDaily highlights, the potential benefit to patients with hereditary diseases is immense. With continued research, the possibilities are truly boundless.